LSDS FOR DUMMIES

(2014) A chaperone enhances blood α‐glucosidase action in Pompe condition sufferers addressed with enzyme replacement therapy. Mol Ther(2015) A murine Niemann‐Decide on C1 I1061T knock‐in product recapitulates the pathological options of essentially the most commonplace human ailment allele. J NeurosciMore than two hundred lysosomal‐reside